Tag: Clinical Trial

  • Breakthrough CRISPR Technology Enables First Human Gene Repair Trial

    Breakthrough CRISPR Technology Enables First Human Gene Repair Trial

    CRISPR technology reached a historic milestone in late 2023 when the Food and Drug Administration (FDA) granted its first approval for clinical application . This groundbreaking authorization marked a pivotal moment in genetic medicine, allowing the CRISPR-Cas9 drug Casgevy® (exagamglogene autotemcel) to treat both sickle cell disease and transfusion-dependent beta thalassemia . The clinical results…